Cell biologists have a detailed picture for what they think the SMN (survival of motor neurons) protein is doing, and how its deficiency causes problems in SMA patients’ cells. This new work could inform delivery of treatments, they say.
Cell biologists have a detailed picture for what they think the SMN (survival of motor neurons) protein is doing, and how its deficiency causes problems in SMA patients’ cells. This new work could inform delivery of treatments, they say.